• First oral treatment for spinal muscular atrophy nets FDA approval

    1 month ago - By Healio

    The FDA approved risdiplam for patients aged at least 2 months with spinal muscular atrophy, according to an agency press release.
    Risdiplam is the first oral drug approved to treat spinal muscular atrophy.
    “Evrysdi is the first drug for this disease that can be taken orally, providing an important treatment option for patients with , following the approval of the first treatment for this devastating disease less than 4 years ago,” Billy Dunn, MD, director of the Office of Neuroscience in the FDA's Center for Drug Evaluation and
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  • FDA OKs First Oral Treatment for Spinal Muscular Atrophy

    1 month ago - By Medscape

    The FDA has approved risdiplam as the first oral treatment for adults and children at least 2 months of age with spinal muscular atrophy.
    FDA Approvals
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  • Oral Treatment OK'd for Rare Neurological Disease

    Oral Treatment OK'd for Rare Neurological Disease

    1 month ago - By MedPageToday

    WASHINGTON - The oral drug risdiplam won approval to treat spinal muscular atrophy in adults and children 2 months of age and older, the FDA announced Friday.
    A liquid medicine, risdiplam is administered daily...
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